Detalhe da pesquisa
1.
Neurogenesis in the striatum of the adult human brain.
Cell
; 156(5): 1072-83, 2014 Feb 27.
Artigo
em Inglês
| MEDLINE | ID: mdl-24561062
2.
Dynamics of oligodendrocyte generation and myelination in the human brain.
Cell
; 159(4): 766-74, 2014 Nov 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-25417154
3.
Base editing of haematopoietic stem cells rescues sickle cell disease in mice.
Nature
; 595(7866): 295-302, 2021 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-34079130
4.
Acute Myeloid Leukemia Case after Gene Therapy for Sickle Cell Disease.
N Engl J Med
; 386(2): 138-147, 2022 01 13.
Artigo
em Inglês
| MEDLINE | ID: mdl-34898140
5.
Biologic and Clinical Efficacy of LentiGlobin for Sickle Cell Disease.
N Engl J Med
; 386(7): 617-628, 2022 02 17.
Artigo
em Inglês
| MEDLINE | ID: mdl-34898139
6.
Phenotypic screening of the ReFRAME drug repurposing library to discover new drugs for treating sickle cell disease.
Proc Natl Acad Sci U S A
; 119(40): e2210779119, 2022 10 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-36161945
7.
A macaque clonal hematopoiesis model demonstrates expansion of TET2-disrupted clones and utility for testing interventions.
Blood
; 140(16): 1774-1789, 2022 10 20.
Artigo
em Inglês
| MEDLINE | ID: mdl-35714307
8.
Ex vivo culture resting time impacts transplantation outcomes of genome-edited human hematopoietic stem and progenitor cells in xenograft mouse models.
Cytotherapy
; 2024 Feb 24.
Artigo
em Inglês
| MEDLINE | ID: mdl-38506770
9.
Towards access for all: 1st Working Group Report for the Global Gene Therapy Initiative (GGTI).
Gene Ther
; 30(3-4): 216-221, 2023 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-34493840
10.
Gene therapy for sickle cell disease: moving from the bench to the bedside.
Blood
; 138(11): 932-941, 2021 09 16.
Artigo
em Inglês
| MEDLINE | ID: mdl-34232993
11.
Lovo-cel gene therapy for sickle cell disease: Treatment process evolution and outcomes in the initial groups of the HGB-206 study.
Am J Hematol
; 98(1): 11-22, 2023 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-36161320
12.
Longitudinal neurocognitive effects of nonmyeloablative hematopoietic stem cell transplant among older adolescents and adults with sickle cell disease: A description and comparison with sibling donors.
Neuropsychol Rehabil
; : 1-20, 2023 Aug 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-37540620
13.
Genome editing strategies for fetal hemoglobin induction in beta-hemoglobinopathies.
Hum Mol Genet
; 29(R1): R100-R106, 2020 09 30.
Artigo
em Inglês
| MEDLINE | ID: mdl-32406490
14.
Optimizing haematopoietic stem and progenitor cell apheresis collection from plerixafor-mobilized patients with sickle cell disease.
Br J Haematol
; 198(4): 740-744, 2022 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-35737751
15.
Risk score to predict event-free survival after hematopoietic cell transplant for sickle cell disease.
Blood
; 136(5): 623-626, 2020 07 30.
Artigo
em Inglês
| MEDLINE | ID: mdl-32518950
16.
Non-myeloablative human leukocyte antigen-matched related donor transplantation in sickle cell disease: outcomes from three independent centres.
Br J Haematol
; 192(4): 761-768, 2021 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-33534948
17.
Allogenic hematopoietic stem cell transplantation in sickle cell disease.
Transfus Apher Sci
; 60(1): 103057, 2021 Feb.
Artigo
em Inglês
| MEDLINE | ID: mdl-33485798
18.
Motivations and Decision-Making of Adult Sickle Cell Patients in High-Risk Clinical Research.
Biol Blood Marrow Transplant
; 26(6): 1225-1232, 2020 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-32200120
19.
Curative options for sickle cell disease: haploidentical stem cell transplantation or gene therapy?
Br J Haematol
; 189(3): 408-423, 2020 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-32034776
20.
Sleep disturbance in adults with sickle cell disease: relationships with executive and psychological functioning.
Ann Hematol
; 99(9): 2057-2064, 2020 Sep.
Artigo
em Inglês
| MEDLINE | ID: mdl-32458066